Director Transporter Sciences BioIVT Boxborough, Massachusetts
This presentation will provide a general overview of this AAPS Gene Therapy Workshop with some basic concepts and introduce the cutting-edge scientific topics that will be addressed by the current experts in this field.
Understand the basic concepts of gene therapy and the current sciences being developed in this modality.
Understand the therapeutic areas gene therapy is targetting and approaches for this modality.
Understand the regulatory and manufacturing challenges of gene therapy and how these challenges may impact development and delivery to patients.